Active Ingredient(s): Elosulfase Alfa
FDA Approved: * February 14, 2014
Pharm Company: * BIOMARIN PHARM

Morquio syndrome, also known as Mucopolysaccharidosis Type IV (MPS IV), is a rare metabolic disorder in which the body cannot process certain types of sugar molecules called glycosaminoglycans (AKA GAGs, or mucopolysaccharides). In Morquio syndrome, the specific GAG which builds up in the body is called keratan sulfate. This birth defect, which is autosomal recessive, is a type of lysosomal storage disorder. The buildup of GAGs in different parts of the body causes symptoms in many different ... [wikipedia]

* May have multiple approval dates, manufacturers, or labelers.

Dosage List

Vimizim 5 mg/5ml Intravenous Injection, Solution, Concentrate
NDC: 68135-100
Biomarin Pharmaceutical Inc.