Active Ingredient(s):Alglucosidase Alfa FDA Approved: * May 24, 2010 Pharm Company: *GENZYME Category:Enzymes
Alglucosidase alfa, sold under the brand name Myozyme among others, is an enzyme replacement therapy (ERT) orphan drug for treatment of Pompe disease (Glycogen storage disease type II), a rare lysosomal storage disorder (LSD).
Chemically speaking, the drug is an analog of the enzyme that is deficient in patients affected by Pompe disease, alpha-glucosidase. It is the first drug available to treat this disease.
It was approved for medical use in the United...
* May have multiple approval dates, manufacturers, or labelers.
Lumizyme 5 mg/ml Intravenous Injection, Powder, for Solution