Active Ingredient(s):Nitisinone FDA Approved: * January 18, 2002 Pharm Company: *SWEDISH ORPHAN Category:Genetic Disorders
Nitisinone, sold under the brand name Orfadin among others, is a medication used to slow the effects of hereditary tyrosinemia type 1 (HT-1).
2 Adverse effects
3 Mechanism of action
7 External links
Nitisinone is used to treat hereditary tyrosinemia type 1 (HT-1) in patients from all ages, in combination with dietary restriction of tyrosine and phenylalanine.[medical citation needed]
Since its first use for this ind...
* May have multiple approval dates, manufacturers, or labelers. 4 Discussions