Active Ingredient(s):Galsulfase FDA Approved: * May 31, 2005 Pharm Company: *BIOMARIN Category:Enzymes
Enzyme replacement therapy (ERT) is a medical treatment which replaces an enzyme that is deficient or absent in the body. Usually, this is done by giving the patient an intravenous (IV) infusion of a solution containing the enzyme.
ERT is available for some lysosomal storage diseases: Gaucher disease, Fabry disease, MPS I, MPS II (Hunter syndrome), MPS VI and Pompe disease. ERT does not correct the underlying genetic defect, but it incr...
* May have multiple approval dates, manufacturers, or labelers.