Golodirsen OverviewGolodirsen, sold under the brand name Vyondys 53, is a medication used for the treatment of Duchenne muscular dystrophy (DMD) in people who have a confirmed mutation of the dystrophin gene that is amenable to exon 53 skipping. The drug was developed by Sarepta Therapeutics. It works by inducing exon skipping in the dystrophin gene and thereby increasing the amount of dystrophin protein available to muscle fibers. The most common side ef...
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Details May Include Instructions, Side Effects, Interactions, Etc. Drug monograph is from Wikipedia. All text is available under the terms of the GFDL (GNU Free Documentation License). Source: en.wikipedia.org/wiki/Golodirsen
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Possible Dosages for this and Related Drugs:
- Solution: 50mg/ml
Other drugs which contain Golodirsen or a similar ingredient: (1 result)
- VYONDYS 53 Golodirsen