Golodirsen

Golodirsen, sold under the brand name Vyondys 53, is a medication used for the treatment of Duchenne muscular dystrophy (DMD).[2] It is an antisense oligonucleotide drug of phosphorodiamidate morpholino oligomer (PMO) chemistry.[1][3] The most common side effects include headache, fever, fall, cough, vomiting, abdominal pain, cold symptoms (nasopharyngitis) and nausea.[2][1] Contents 1 Medical uses 2 Mechanism o... [wikipedia]